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News

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FORGE meets with SULIS THERAPEUTICS

FORGE meets Sulis Therapeutics to discuss new STING-targeted therapy On 3rd February
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Gene Therapy for Deadly Blood Disorder Restores Function in Patients’ Cells

Recent advances in in-utero blood transfusion technology have made it possible for
News article 2 mins read

Targeted treatment for  rare, inherited immunodeficiency Activated PI3-Kinase delta syndrome (APDS)

A teenager has become the first patient in the UK and Europe
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Children cured of genetic blindness

Doctors in London have become the first in the world to cure
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New gene treatment for Haemophilia B available on NHS

A gene therapy treatment for haemophilia B that costs £2.6 million per
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A baby girl born deaf treated with pioneering new gene therapy at Cambridge University NHS Trust.

A baby girl born deaf because of a rare genetic mutation in
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First in the world gene-editing treatment for sickle cell disease and beta thalassaemia

UK medicine’s regulator approved the first in the world gene-editing treatment for


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