Article type:
News
Estimated read time:
1 min min read
Published:
15/05/2024
A baby girl born deaf because of a rare genetic mutation in the OTOF gene became the youngest patient in the world to be treated with pioneering new gene therapy at Cambridge University NHS Trust. Within four weeks of having the gene therapy, Opal, who was born completely deaf, responded to sound and at 24 weeks had normal hearing levels. The CHORD trial which started in May 2023 is ongoing and producing spectacular results for these children.